gene therapy
Single-Dose CaBP4 Gene Therapy Rewired Adult Dog Retinas and Rebuilt the Synaptic Layer That Never Formed
Health News
October 5, 2026
Single-Dose CaBP4 Gene Therapy Rewired Adult Dog Retinas and Rebuilt the Synaptic Layer That Never Formed
One CaBP4 viral dose restored dim-light vision in adult dogs and thickened a retinal synapse that development never finished. Ribbons grew toward normal length.
Sebastien Beauzile Is Pain-Free After Lyfgenia While a $3.1 Million Sickle Cell Therapy Still Barely Reaches Patients
Health News
March 14, 2025
Sebastien Beauzile Is Pain-Free After Lyfgenia While a $3.1 Million Sickle Cell Therapy Still Barely Reaches Patients
Sebastien Beauzile left sickle cell pain behind after Lyfgenia at Cohen Children's. Fewer than 40 patients have been infused, and the $3.1 million price still blocks the door.